This scheme provides funding for established researchers and teams from any discipline who want to pursue bold and creative research ideas to deliver significant shifts in understanding that could improve human life, health and wellbeing.
View this resource Bookmark this resourceAward
Christopher Duncan Horn Memorial Award
Published by Muscular Dystrophy Association National Office
AwardDuchenne Muscular DystrophyDMDMDA has invested over $125M in the development of gene therapy for neuromuscular diseases (NMDs) over the past 20 years. To continue to lead the way in this important field of medicine, MDA held a summit in January 2022 to address the challenges in safely delivering AAV-based gene replacement therapy to NMD patients. In this meeting, top experts and stakeholders convened to talk openly about adverse events linked to clinical trials in the field. Although experts collectively agree that gene therapy holds great promise in addressing the underlying cause of many neuromuscular diseases, there are still many challenges and risks that must be overcome to fully realize the translational potential of gene therapy in NMDs affecting children and adults.
View this resource Bookmark this resource
Transformative Research Award: Retinal Degeneration
Published by Fighting Blindness Canada
AwardRetinal DegenerationFighting Blindness Canada is launching the Transformative Research Award (TRA) program to fund strategic areas of need within vision research.
The 2022/23 competition will fund innovative and ambitious research that will advance the development of new therapies for retinal degenerative diseases. This competition is open to discovery, translational or clinical research. The program is open to Canadian or international investigators, with a budget of up to $1.25 million over five years per award. This competition has two stages: Letter of Intent and Full Application (by invitation only).
View this resource Bookmark this resource
Recordati Rare Disease
Published by RECORDATI
PrivateAwardBasic ResearchClinical ResearchPreclinical ResearchIndustrial Development or SMEGrantFellowship
2021 Research Grant Merck
Published by MERCK GROUP
PrivateAwardBasic ResearchClinical ResearchPreclinical ResearchIndustrial Development or SMEGrantFellowshipInternational
FONDATION MALADIES RARES (FFRD)
Published by FONDATION MALADIES RARES
PrivateAwardBasic ResearchClinical ResearchPreclinical ResearchIndustrial Development or SMEGrantFellowshipsFrench Foundation for Rare Diseases (FFRD) is a non-profit organization of scientific cooperation. Its missions are to accelerate research for all rare diseases by supporting research and researchers.
View this resource Bookmark this resource
FONDAZIONE PUGLIA
Published by FONDAZIONE PUGLIA
PrivateAwardBasic ResearchPreclinical ResearchFoundationGrantFellowshipPuglia Foundation, is a private legal entity and has full statutory and managerial autonomy. It originates from the Cassa di Risparmio di Puglia
View this resource Bookmark this resourceTelethon is a non-profit organization recognized by the Ministry of University and Scientific and Technological Research.
View this resource Bookmark this resource
Private funding
Published by IRDiRC
Rare DiseaseCrowdfundingPrivateFoundations or DonationsAwardLoanVenture Capital or Angel InvesmentList of different kinds of private funding available for orphan drug development.
View this resource Bookmark this resource