The aim of the mentoring is to increase the impact and patient benefit of the excellent science funded in EJP RD, by providing tailored expertise along each step of the translational pathway. This expertise is delivered early on at the project proposal phase so that the route to patient impact can be planned out. This greatly reduces the barriers between promising science and accessible treatments.
With this mentoring support, applicants will receive project-specific feedback from a panel of drug development, biomarker validation, methodological and regulatory experts tasked with optimizing the translational feasibility of the study. There are no costs or obligations to the researcher.
The Mentoring programme is available to any scientist working on, or planning to work on, a translational research project in rare diseases. The mentoring itself has been organized into three packages:
- Package one is for researchers planning to apply for funding
- Package two is for shortlisted second- stage proposals of a rare disease funding call
- Package three is for researchers that have received funding
The packages consist of short videos and the possibility to schedule virtual one-on-one meetings with a mentor to discuss specific questions related to your research proposal
Related Resources
The aim of the mentoring is to increase the impact and patient benefit of the excellent science funded in EJP RD. With this mentoring support, applicants will receive project-specific feedback from a panel of drug development, biomarker validation, methodological and regulatory experts tasked with optimizing the translational feasibility of the study. There are no costs or obligations to you.
View this resource Bookmark this resourceThe topics of mentoring span from translational feasibility, therapy development, manufacturing of drug to carry out non-clinical experiments and later clinical trials, product classification, suitability of analytical readouts, quality assurance and control, regulatory compliance, intellectual property strategy, data and innovation management. Our experience thus far is that the latter four topics have been in most demand.
The mentors are a panel of drug development, biomarker validation, methodological and regulatory experts, many of them with an industry background coming from the extensive networks of the partners in the EJP RD. These networks include those of the ESFRI infrastructures (BBRMI, ECRIN, EATRIS, ELIXIR), the European Reference Networks (ERNs), global partners in and outside of IRDiRC (especially those with drug, medtech and diagnostics development expertise, such as NIH NCATS, CDRD, LifeArc, AFM Telethon, FTELE), and the paediatric research community through CVBF-EPTRI. The mentors work pro-bono under full confidentiality and give project-specific feedback. There are no costs or obligations to the researcher. Experts will mentor teams in a longitudinal, distance format, via regular conference call meetings and occasional face-to-face meetings as needed, and will verify the achievement of milestones, advise on further steps and issue recommendations on technical progress, to maximize the project’s potential of success and further development towards the clinic.
What do the mentors say about this service?
Package one can be accessed by researchers planning to apply for funding. The package consists of a series of short videos which you can watch at your own pace. The topics addressed below are the most frequently asked questions we receive during proposal preparation phase and mostly related to non-scientific topics. The videos will help you develop a robust translational research plan and strengthen your proposal.
Related Resources
This is TREAT-NMD webpage, where it can be found relevant information how to find biomaterials for The basic scientific research being carried out on Neuromuscular Diseases. It can work also as inspiration for investigators conduting reasech in others rare diseases
View this resource Bookmark this resourcePackage two covers the second stage of a rare disease funding call and provides support for researchers who are writing a proposal for innovation and translation in a regulatory compliant manner. This package consists of both videos and the possibility to schedule virtual one-on-one meetings with a mentor to discuss specific questions related to your research proposal.
Related Resources
Package three is for researchers that have received funding. The last package consists of videos and virtual one-on-one meetings with a mentor. In these mentoring meetings, applicants will receive project-specific feedback from a panel of drug development, biomarker validation, methodological and regulatory experts tasked with optimizing the translational feasibility of the study.
Testimonial from a scientist who has used our expert mentoring service
Related Resources
The aim of the mentoring is to increase the impact and patient benefit of the excellent science funded in EJP RD. With this mentoring support, applicants will receive project-specific feedback from a panel of drug development, biomarker validation, methodological and regulatory experts tasked with optimizing the translational feasibility of the study. There are no costs or obligations to you.
View this resource Bookmark this resourceThis is TREAT-NMD webpage, where it can be found relevant information how to find biomaterials for The basic scientific research being carried out on Neuromuscular Diseases. It can work also as inspiration for investigators conduting reasech in others rare diseases
View this resource Bookmark this resource