Development of new effective therapies for rare diseases

Published by European Commission

GrantRare Disease

This topic aims at supporting activities that are enabling or contributing to one or several expected impacts of destination 3 “Tackling diseases and reducing disease burden”. To that end, proposals under this topic should aim for delivering results that are directed, tailored towards and contributing to some of the following expected outcomes:

Researchers and developers make the best use of the state-of-the-art knowledge and resources for a fast and effective development of new therapies for rare diseases.
Researchers and developers increase the development success rate of therapies for rare diseases by employing robust preclinical models, methods, technologies, validated biomarkers, reliable patient reported outcomes and/or innovative clinical trials designs.
Developers and regulators move faster towards market approval of new therapies for rare diseases (with currently no approved treatment option) due to an increased number of interventions successfully tested in late stages of clinical development.
Healthcare professionals and people living with a rare disease get access to new therapeutic interventions and/or orphan medicinal products.

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Research Grants for Angelman Syndrome

Published by Angelman Syndrome Foundation

GrantAngelman Syndrome

The ASF Scientific Advisory Committee identified the following areas of unmet need in AS research. Priority will be given to the following topics:

Projects studying or correcting the heterozygous effect of non-UBE3A genes in deletion.
Projects studying the potential results of increasing UBE3A after therapies or for some subtypes of AS.
Projects studying delivery of therapies and potential for improvement.
Symptomatic therapies that impact the daily life of people with Angelman syndrome and their families.
Proposals that do not address these topics are still welcome and will be given full consideration.

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European Society for Immunodeficiencies (ESID) Bridge Grant

Published by European Society for Immunodeficiencies

Primary ImmunodeficiencyGrant

ESID wants to invest in the future of researchers and clinicians committed to PIDs. Therefore ESID Bridge Grants aim to allow trainees working on PIDs to continue their activity in the field of PID in their institution or another institution during short periods of time until they can find other financial sources, thus avoiding the interruption of their training process.

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ALS Association’s Seed Grants

Published by ALS Association


For this funding opportunity The ALS Association will accept applications from all scientific disciplines on topics that have the potential to ultimately transform the experience of ALS, by optimizing the care and treatments we have, finding new treatments and cures, and or preventing ALS. In addition to projects focused on ALS, projects that investigate the continuum of disease spanning ALS and FTD are in scope

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Research Grant for Rett Syndrome

Published by International Rett Syndrome Foundation

Rett SyndromeGrant

IRSF believes that research into a variety of Rett and Rett-related topics is necessary to create treatments and eventual cures for every individual living with Rett syndrome. We proudly invest in such research at every stage: from basic science that can change the way we think about MeCP2 to clinical research that directly impacts potential treatments. We also help connect Rett researchers with external funding opportunities.

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Prader-Willi Research Grant

Published by Foundation for Prader-Willi Research

GrantPrader-Willi syndromePWS

The Foundation for Prader-Willi Research (FPWR) is dedicated to supporting research to advance the understanding and treatment of Prader-Willi syndrome (PWS). We invite applications for funding on an annual or semiannual basis, in response to a Request for Applications.

FPWR accepts applications in all areas of research relevant to PWS, but we are particularly interested in supporting projects that will lead to new interventions to alleviate the symptoms associated with PWS. FPWR accepts applications from academic, government, non-profit or for-profit research entities. Academic research applicants should have a primary faculty appointment at the level of Instructor or higher. This grant program will be useful for junior faculty in the early stages of their careers, established investigators in other areas of research who wish to enter the field of PWS research, or investigators in the PWS field who are seeking funding to support pilot studies in a new area of PWS research. FPWR seeks to support innovative, high-risk/high reward research in its early stages

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