How do I identify and validate the right disease target?

What are the main mechanisms and tools to search a hit compound?

How do I validate a small molecule lead compound?

How do I optimize a lead compound?

How do I create the formulation and scalability of a lead compound?

How do I choose the right disease model?

How do I develop my biomarker strategy?

Why is the Natural History so important in rare diseases?

What are the main challenges to develop repurposed drugs?

What are the main bottlenecks for advanced therapies for reaching patients?